2009 DNA Therapies 
The Pharma Data
DECEMBER 11, 2020
11, 2020 — Results from a long-term study of a gene therapy technique to prevent inherited mitochondrial disease show promise, researchers say. The researchers said the technique could break the cycle of disease passed from mother to baby through mutations in mitochondrial DNA (mtDNA). FRIDAY, Dec. in the small intestine.
The Pharma Data
OCTOBER 21, 2020
In the midst of the global pandemic, the analysis found no antiretroviral therapy interruptions across the entirety of the ongoing clinical development programme for long-acting cabotegravir and rilpivirine. Of those participants who transitioned back to injectables, the median duration of oral therapy was 51 days.
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DrugBank
JUNE 27, 2023
Their use, as well as their integration into other types of data, has enabled the development of more precise therapies. In contrast, non-coding mutations have effects on gene expression, transcript stability, and the physical state of the DNA itself (e.g., 5 , e1000433 (2009). PLoS Genet. Kennedy, A. Ozbek, U. &
The Pharma Data
JUNE 24, 2021
The study will evaluate the efficacy and safety of talazoparib, an oral poly (ADP-ribose) polymerase (PARP) inhibitor, in combination with enzalutamide, an androgen receptor inhibitor, compared with placebo plus enzalutamide in men with DNA damage response (DDR)-deficient metastatic castration-sensitive prostate cancer (mCSPC).
PLOS: DNA Science
OCTOBER 17, 2024
The new drug is taken with miglustat , which FDA approved for use in NPD3 in 2009. Until today, there were no approved therapies in the US. The post New Drug Miplyffa Approved for Rare Niemann-Pick Disease Type 3 appeared first on DNA Science. The original approved was in 2003 to treat a type of Gaucher disease.
Codon
APRIL 9, 2023
” — Harold Morowitz 🔥 Ten Amazing Things (that happened this week…) A CAR-T therapy was tested in 27 children with neuroblastomas. Thousands of transcription factors — proteins that bind DNA and control gene expression — were studied in human cells. Molecular Therapy. Gene Therapy.
Codon
JULY 21, 2024
As the biotechnologist Alex Telford writes , “Without mouse models, we may never have developed polio and meningitis vaccines, organ transplants, GLP-1 drugs, gene therapies , or any other number of transformative treatments.” In 1959, before DNA sequencing, temperamentally-wild foxes used in the fur trade were bred for tameness.
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