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THE LANCET HAEMATOLOGY: Global, regional, and national prevalence and mortality burden of sickle cell disease, 2000–2021

SCIENMAG: Medicine & Health

Credit: The Lancet Journal The Lancet Haematology Article Title Global, regional, and national prevalence and mortality burden of sickle cell disease, 2000–2021: a systematic analysis from the Global Burden of Disease Study 2021 Article Publication Date 15-Jun-2023

Disease 84
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Belfast techbio raises £1.4m to tackle complex diseases

Drug Discovery World

The company, which is a spin-out from the Queen’s University Belfast, was established in 2021 to commercialise a drug discovery platform developed by researchers in the School of Biological Science at Queen’s. AMPLY works with a network of disease and biotech partners to help advance its programmes.

Disease 147
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UK lags behind on access to treatments for rare diseases

Drug Discovery World

The UK lags comparable countries, including France and Germany, on the degree of availability of treatments for rare diseases, according to a new report. The report by the BIA and consultancy firm PwC has highlighted the progress that has been made in improving access to rare disease treatments in the UK, and the challenges that remain.

Disease 130
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Which diseases are poised to benefit from therapeutic antibody development

Drug Discovery World

DDW’s Megan Thomas looks at how different diseases will benefit from the success of therapeutic antibodies. billion in 2021, and is projected to reach $106.8 The work is continuous for this disease target. Cancer Monoclonal antibodies (mAbs) are a type of targeted drug therapy, and as such are often used to treat cancer.

Disease 147
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With new IPO pitch, Artiva touts ‘natural killer’ cell therapy for autoimmune disease

BioPharma Drive: Drug Pricing

Like many of its cell therapy peers, Artiva, which originally sought an IPO in 2021, has shifted its strategy in hopes of riding a recent wave of investor interest in autoimmune disease research.

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European coalition to accelerate research into 7000 rare diseases

Drug Discovery World

The ‘Rare Disease Moonshot’, a new initiative to boost research and development into rare and paediatric diseases, has launched at the European Health Summit. . It aims to speed up research into more than 7000 identified rare diseases, of which a staggering 95% have no approved treatment or cure. .

Disease 130
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Rhythm Pharmaceuticals buys biotech focused on rare disease

Drug Discovery World

CHI is a rare genetic disease in which cells secrete excess insulin, causing hypoglycemia, which can result in serious health outcomes including seizures, coma, permanent brain damage and death. Xinvento is developing novel investigational therapeutic candidates designed to improve the care of patients with CHI.

Disease 130