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Scientific workflow for hypothesis testing in drug discovery: Part 2 of 3

Drug Target Review

Raminderpal earned his PhD in semiconductor modelling in 1997 and has published several papers and two books and has twelve issued patents. He was also Vice President and Head of the Microbiome Division at Eagle Genomics Ltd, in Cambridge.

Drugs 69
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Sloane’s Journey with ASO Therapy

KIF1A

She is scheduled to be the 2nd patient in the world to receive ASO therapy for KAND. March 2023 – We met with n-Lorem and found out Susannah’s ASO (1st KAND patient to receive ASO therapy for KAND) would work for Sloane. We want to be an open book during this process. Sloane is an adorable 3 year old with KAND.

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Topical Gene Therapy FDA-Approved for Severe Skin Disease, Dystrophic Epidermolysis Bullosa

PLOS: DNA Science

The newest FDA-approved gene therapy treats the severe, skin-peeling condition dystrophic epidermolysis bullosa (DEB). The gene treatment has been a long time coming, but it differs from the handful of other approved gene therapies: it isn’t a one-and-done. DEB has been a candidate for a gene therapy since 2002.

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Scientific workflow for hypothesis testing in drug discovery: Part 1

Drug Target Review

He has published several papers and two books and has twelve issued patents. He was also Vice President and Head of the Microbiome Division at Eagle Genomics Ltd, in Cambridge. Raminderpal earned his PhD in semiconductor modelling in 1997.

RNA 52
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Debunking 3 Common Schizophrenia Myths

Olympian Clinical Research

Like many other mental illnesses, Schizophrenia – when portrayed in TV, movies, or even books – is often misrepresented, and the effects are incredibly damaging to the men and women who are struggling daily with the condition. . The disease is more common than many may realize, with approximately 2.6

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Takeda to sell another non-core portfolio for $260 million to Cheplapharm

The Pharma Data

Takeda has revealed it has agreed to divest its non-core portfolio of prescription therapies to Cheplapharm in exchange for an upfront payment of $562 million. The moves represent Takeda’s attempts to balance the books following its mammoth acquisition of Shire in 2018 for $62 billion. Matt Fellows. Source link.

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Game-changing pan-TEAD inhibitor for solid tumours

Drug Target Review

TEAD proteins are known to be very important in cancer progression TEAD proteins are known to be very important in cancer progression, and there are a number of therapies in development. Can you provide a summary of the key findings and implications of the preclinical studies on ISM6331 for the treatment of advanced solid tumours?