Drug Discovery World
OCTOBER 18, 2023
Adeno-associated virus (AAV) vector-based gene therapies hold exceptional promise across a range of disease areas. Promising therapies are stumbling in clinical trials AAV vector-based gene therapies use modified viruses as drug delivery vehicles to effectively introduce DNA sequences into cells via transduction. She received a Ph.D.
KIF1A
MAY 24, 2023
In this blog post, KIF1A.ORG Chief Science Officer Dr. Dominique Lessard describes a unique cross disciplinary experience with multiple scientific stakeholders in the rare disease space, all focused around our holistic understanding of KAND. How do we move the needle to make patient voices and experiences the center of scientific discovery?
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Drug Target Review
JANUARY 30, 2024
About the author Dr Jia-Jia Zhang, Doctoral candidate Dr Jia-Jia Zhang is a doctoral candidate at the National Translational Science Center for Molecular Medicine & Department of Cell Biology, Fourth Military Medical University, and her research interest is the development of therapeutical antibodies to treat human disease.
Drug Target Review
JANUARY 31, 2024
Early in my education, I developed an interest in understanding how chemical entities derived from natural resources could be modified and used to fight specific diseases.
Drug Discovery World
APRIL 14, 2023
He is being recognised for his revolutionary contributions to developing the first gene-edited cell-based therapy for cancer that involves the genetic re-engineering of a patient’s own T cells to combat their disease, and for demonstrating that adoptive T-cell therapy can induce remission and in some cases cure patients with advanced cancer.
Codon
APRIL 9, 2024
“Cumulatively the deadliest of the human infectious diseases,” malaria has been documented throughout recorded history. In this light, scouring old Chinese remedies for new treatments for a disease specifically troublesome during war was entirely intuitive for Chinese biomedical scientists like Tu Youyou in the mid-20th century.
Broad Institute
OCTOBER 11, 2023
By Allessandra DiCorato October 11, 2023 In 2011, Robert Manguso was working in a cell biology lab when his mother was diagnosed with Merkel cell carcinoma, a rare and aggressive skin cancer. His mother had a presentation of the disease that suggested her immune system was already on the job.
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