Drug Research, Drug Trials, Pharmaceuticals and Therapies

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Drug Research

Drug Trials

Pharmaceuticals

Therapies

An Evolving Regulatory Environment for Rare and Orphan Diseases

Advarra

AUGUST 16, 2022

The Orphan Drug Act of 1983 was instrumental in changing the number of orphan drugs approved in the U.S. The law established the Office of Orphan Products Development , providing financial incentives for pharmaceutical companies to develop orphan drugs and making it more viable to invest in orphan drug research and development.

Disease

Disease Clinical Trials FDA Approval FDA

Deliberate Dysentery

Codon

JANUARY 21, 2024

We wouldn't do a challenge trial for Ebola, because the disease is extremely severe, and there are currently no licensed treatments or vaccines. You can do a challenge trial with deadly diseases, but you need a “rescue therapy.” There have been deaths in phase 1 medical and drug research among healthy participants.

Vaccine

Vaccine Trials Disease Virus

Drug Discovery Digest

An Evolving Regulatory Environment for Rare and Orphan Diseases

Deliberate Dysentery

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