Drugs and Therapies - Drug Discovery Digest

Drug candidate eliminates breast cancer tumors in mice in a single dose

Science Daily: Pharmacology News

JANUARY 22, 2025

Treatment typically involves surgery and follow-up hormone therapy, but late effects of these treatments include osteoporosis, sexual dysfunction and blood clots. Despite significant therapeutic advances, breast cancer remains a leading cause of cancer-related death in women.

Treatment

Treatment Therapies Drugs Research

Sarepta scraps a Duchenne drug as gene therapy sales rise

BioPharma Drive: Drug Pricing

NOVEMBER 7, 2024

Elevidys sales have increased since the FDA made a controversial choice to expand the therapy's use. Now, Sarepta is abandoning a successor to its drug Exondys 51, citing an “evolving" treatment landscape.

Drug candidate eliminates breast cancer tumors in mice in a single dose

Sarepta scraps a Duchenne drug as gene therapy sales rise

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Combo Therapy May Be Advance Against Liver Cancer

Pfizer hemophilia gene therapy arrives in US to uncertain future

FDA Approves Landmark Sickle Cell Gene Therapies, Casgevy and Lyfgenia

Secondary Tumors After CAR-T Cancer Therapies Are Rare: Study

FDA Warns of Rare Secondary Cancer Risk With CAR-T Therapies

Synthesis and Investigation of Peptide–Drug Conjugates Comprising Camptothecin and a Human Protein‐Derived Cell‐Penetrating Peptide

FDA Approves First Gene Therapy, Elevidys, to Treat Duchenne Muscular Dystrophy

FDA Approves Landmark Sickle Cell Gene Therapies

Precision sells lymphoma drug to Imugene in retreat from cell therapy research

FDA sets advisory meeting date for Brainstorm’s ALS cell therapy

FDA Approves First Gene Therapy to Treat Duchenne Muscular Dystrophy

FDA Advisors Say New Gene Therapy for Sickle Cell Disease, Exa-cel, is Safe

Royalty Pharma buys into Ferring’s cancer treatment in first gene therapy deal

Combo Therapy Boosts Survival for Advanced Colon Cancer

So, Who Benefits From New Cancer Drugs?

CG follows big IPO with new results for bladder cancer drug

Scientists develop grain-sized soft robots controlled by magnetic fields for targeted drug delivery

FDA Says No to MDMA as Therapy for PTSD

Judo Bio debuts with $100M and a plan to take RNA drugs to the kidney

Statin therapy may prevent cancer by blocking inflammatory protein

New cell therapy model accelerates cancer treatment development

New drug triggers rapid cell death in cancer models

Two-Drug Treatment Could Curb Meth Addiction

Bayer partners with RNA drugmaker to develop new cancer therapies

IGM’s autoimmune pivot backfires as top drug disappoints in testing

Sickle cell patient dies in Beam study of base editing therapy

Cancer cell therapy from Arcellx, Gilead shows promise in early data

FDA Approves First Gene Therapy for Severe Hemophilia A, Roctavian

CRISPR therapy from Intellia may ameliorate rare heart disorder, data suggest

ALS drug from Denali, Sanofi falls short in mid-stage study

Atalanta banks $97M to send RNAi drugs into the brain

Lilly gene therapy finding puts focus on hearing loss treatment pipeline

New Combo Drug Therapy Halves Death Risk From Advanced Hodgkin Lymphoma

Gene therapy startup emerges with green light for first-of-its-kind trial

Gilead to lay off staff at cell therapy unit Kite

BioMarin drops drug programs in pipeline cull

Ajax, aiming for a better JAK drug, raises $95M to begin first tests

European regulators want to know more about the risks of GLP-1 drugs

Sarepta sells FDA fast pass earned from Duchenne gene therapy approval

Scholar Rock scores with ‘surprise’ success in SMA drug study

Bayer says menopause drug succeeds in breast cancer study

Roche reports survival data for new dual-acting lymphoma drug

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