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New insights into the role of viral capsids in gene therapy safety

Drug Target Review

Viral vectors have been crucial in transforming the gene therapy landscape due to their natural ability to infect cells. 1 In 2017, the US Food and Drug Administration (FDA) approved the first AAV-based gene replacement therapy (Luxturna), for Leber congenital amaurosis type 2.

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Hansa Biopharma to present at the 39th Annual J.P. Morgan Healthcare Conference

The Pharma Data

Imlifidase is additionally being evaluated for further use in other transplantation indications as well as investigated in autoimmune indications and as a pretreatment in gene therapy for inactivation of neutralizing antibodies. Vator Swiss-Nordic Healthcare Seminar on Thursday February 11, 2021.

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Article EMA Thank You What we expect European regulators to do in May 2024

Agency IQ

Two consultations on clinical trial considerations, one on advanced therapies and the other addressing non-inferiority and equivalence comparisons, are closing at the end of May. Start Date End Date Event Event Type Organization 4/30/2024 4/30/2024 Seminar No. The pharma reform package remains in E.U.

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Women in Stem with Dr Rachel Lagiakos

Drug Target Review

At CTx, Rachel’s contributions to pioneering work drugging novel epigenetic targets led to a first-in-class asset in the clinic targeting ER+ breast cancer, including patients refractory to endocrine therapy. As a woman in STEM, what unique perspectives or strengths do you believe you bring to your work?

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Why Content Is the Key to Opening Healthcare’s Digital Front Door – Part 2: Payers

Perficient: Drug Development

But, occasionally, you’ll want to motivate users to fill out a form, download an e-book, sign up for a seminar or any number of other related activities. Make it easy for them to verify your claims no matter how they’re interacting with you. Of course, most of your conversion activities should be geared toward shopping for a health plan.

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#ScienceSaturday: March 9, 2024

KIF1A

This spring we’ve been quite fortunate to be joined by 6 Master’s students from Columbia University, who have been contributing to our creation of community resources as part of their Seminar in Biotechnology Course. Researchers have used a variety of cellular tests to model HSPs in iPSC models.

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Article EMA Thank You What we expect European regulators to do in April 2024

Agency IQ

regulatory framework Webinar/ Seminar ( OPEN ) EMA 4/17/2024 4/17/2024 CEP 2.0: regulatory framework Webinar/ Seminar ( OPEN ) EMA 4/17/2024 4/17/2024 CEP 2.0: regulatory framework Webinar/ Seminar ( OPEN ) EMA 4/17/2024 4/17/2024 CEP 2.0: regulatory framework Webinar/ Seminar ( OPEN ) EMA 4/17/2024 4/17/2024 CEP 2.0: